Inherited neuromuscular diseases : translation from pathomechanisms to therapies /

Bibliographic Details
Corporate Authors: International Symposium on Rare Diseases Valencia, Spain, SpringerLink (Online service)
Other Authors: Espinós, Carmen, Felipo, Vicente, Palau, Francesc
Format: Conference Proceeding eBook
Language:English
Published: Dordecht : Springer, [2009]
Series:Advances in experimental medicine and biology ; v. 652.
Subjects:
Online Access:Connect to the full text of this electronic book
Table of Contents:
  • Pathology and diagnosis of muscular dystrophies / Carmen Navarro, Susana Teijeira, Beatriz San Millán
  • Standards of care for Duehenne muscular dystrophy : brief treat-NMD recommendations / Thomas Sejerson, Kate Bushby on behalf of the TREAT-EU Network of Excellence
  • Genetics and pahtogenesis of distal muscular dystrophies / Bjarne Udd
  • Phenotype variations in early onset Pompe disease : diagnosis and treatment results with Myozyme® / Samuel Ignacio Pascual Pascual
  • Diseases of the human mitochondrial oxidative phosphorylation system / Julio Montoya, Ester López-Gallardo, María Dolores Herrero-Martín, Íñigo Martínez-Romero, Aurora Gómez-Durán, David Pacheu, Magdalena Carreras, Carmen Diéz-Sánchez, Manuel J. López-Pérez, Eduardo Ruiz-Pesini
  • Mitochondrial diseases : a cross-talk between mitrochondrial and nuclear genomes / Antonella Spinazzola, Massimo Zeviani
  • Mitochondrial disorders due to nuclear OXPHOS gene defects / Cristina Ugalde, María Morán, Alberto Blázquez, Joaquín Arenas, Miguel A. Martín
  • Coenzyme Q10 deficiencies in neuromuscular diseases / Rafael Artuch, Leonardo Salviati, Sandra Jackson, Michio Hirano, Plácido Navas
  • The role of mitochondrial network dynamics in the pathogenesis of Charcot-Marie-Tooth disease / Francesc Palau, Anna Estela, David Pla-Martín, Maribel Sánchez-Piris
  • Pathogenesis and treatment of mitochondrial disorders / Salvatore DiMauro, Michio Hirano
  • Biology of peripheral inherited neuropathies : Schwann cell axonal interactions / Michael E. Shy
  • Phenotype and clinical evolution of Charcot-Marie-Tooth disease type 1A duplication / José Berciano, Antonio García, Elena Gallardo, César Ramón, Onofre Combarros
  • Genotypes & sensory pheotypes in 2 new X-linked neuropathies (CMTX3 and dSMAX) and dominant CMT/HMN overlap syndromes / Garth Nichoson, Marina Kennerson, Megan Brewer, James Garbern, Michael Shy
  • Natural history and treatment of peripheral inherited neuropathies / Davide Pareyson, Chiara Marchesi
  • Spinal muscular atrophy during human development : where are the early pathogenic findings? / Eduardo Tizzano
  • Spinal muscular atrophy / Jérémie Vitte, Ruben Attali, Nasim Warwar, Irena Gurt, Judith Melki
  • Friedreich ataxia : an update on animal models, frataxin function and therapies / Pilar González-Cabo, José Vicente Llorens, Francesc Palau, Maria Dolores Moltó
  • Genetics and pathogenesis of inherited ataxias and spastic paraplegias / Carmen Espinós, Francesc Palau.